Impact of mRNA chemistry and manufacturing process on innate immune activation.
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An mRNA Vaccine against SARS-CoV-2 – Preliminary Report.
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An RNA vaccine drives immunity in checkpoint-inhibitor-treated melanoma.
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Efficiency and Target Derepression of Anti-miR-92a: Results of a First in Human Study.
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Single Dose Pharmacokinetics and Pharmacodynamics of Transthyretin Targeting GalNAc-siRNA Conjugate, Vutrisiran, in Healthy Subjects.
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Phase 1-2 Trial of Antisense Oligonucleotide Tofersen for SOD1 ALS.
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Hybridization Liquid Chromatography-Tandem Mass Spectrometry: An Alternative Bioanalytical Method for Antisense Oligonucleotide Quantitation in Plasma and Tissue Samples.
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Increased PIP3 activity blocks nanoparticle mRNA delivery.
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Targeted Delivery of Antisense Oligonucleotides Using Neurotensin Peptide.
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Evolution of abiotic cubane chemistries in a nucleic acid aptamer allows selective recognition of a malaria biomarker.
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