Diverse lipid conjugates for functional extra-hepatic siRNA delivery in vivo
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Cationic Oligospermine-Oligonucleotide Conjugates Provide Carrier-free Splice Switching in Monolayer Cells and Spheroids
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Membrane Destabilization Induced by Lipid Species Increases Activity of Phosphorothioate-Antisense Oligonucleotides
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Protein production is an early biomarker for RNA-targeted therapies
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