Antisense approaches for the treatment of Duchenne muscular dystrophy and recent advances to address DMD brain comorbidities

May 23rd, 2024|Categories: Past Webinars|

Date: May 23, 2024 Time: 8am PDT / 11am EDT / 5pm CEST Title: Antisense approaches for the treatment of Duchenne muscular dystrophy and recent advances to address DMD brain comorbidities Description: This presentation will cover the development of ASO-based approaches ...

Hope of New Treatments for Chronic Liver Disease MASH (NASH)

May 7th, 2024|Categories: Perspectives on Current Science|

In the early stages of Metabolic Dysfunction-Associated Steatohepatitis (MASH), many patients are asymptomatic, though some may feel weak or fatigued or have an ache in their upper right abdomen. While lifestyle changes can help patients diagnosed early enough, more advanced stages of the disease ...

RNA Single-base Editing Therapy that Treats Genetic Lung and Liver Disease Entered Clinical Trials

April 16th, 2024|Categories: Perspectives on Current Science|

When Peggy's mom was in her forties, she started to have trouble breathing. Although she had never smoked, she had been exposed second-hand earlier in her life. Eventually, her mother ended up at the Mayo Clinic, where she was the 36th patient to be ...

FDA Approved the First CRISPR Treatment – Potential Cure for People with Sickle Cell Disease

March 14th, 2024|Categories: Perspectives on Current Science|

Victoria Gray was diagnosed with sickle cell disease (SCD) when she was just three months old; since then, episodes of pain and frequent hospitalizations have been a part of her life. Many of her dreams seemed like far-off impossibilities when the smallest things, like ...

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