New CRISPR Technique May Be the Solution to Replacing Entire Genes

January 4th, 2023|Categories: Featured Perspectives On Current Science|

Ever since it was discovered that CRISPR could be used for genome editing, scientists across the world have been working on creating safe, effective ways to use this incredible tool to cure many different human diseases. From the first CRISPR-Cas system that works as ...

Using CRISPR to Personalize Cancer Immunotherapy Treatment

December 12th, 2022|Categories: Featured Perspectives On Current Science, Perspectives on Current Science|

In 2020, there were an estimated 18.1 million cases of cancer worldwide (excluding non-melanoma skin cancer). Breast, lung, and colorectal cancer were the most common and together contributed to 35.4% of these cases. In the same year, 9.5 million cancer-related deaths were reported. According to ...

Will N-of-1 Drugs Play a Role in the Future of Medicine?

November 22nd, 2022|Categories: Featured Perspectives On Current Science, Perspectives on Current Science|

Throughout the millennia, anyone who had anything beyond a simple illness could only do their best to ease the pain and petition whatever deities their culture believed in. Then, in the past few centuries, medicine and science have advanced to the point that many ...

Centyrins Effectively and Safely Deliver siRNAs to Multiple Muscle Tissues

November 9th, 2022|Categories: Featured Perspectives On Current Science, Perspectives on Current Science|

In 2018, Susan Dillon and Karyn O'Neil knew they had created something special that could change the treatment of genetic diseases. Now, their company’s drug that uses their proprietary technology has been granted orphan drug status by the U.S Food and Drug Administration (FDA). The ...

Reflections following the 20th annual meeting on oligonucleotide therapeutics

November 3rd, 2022|Categories: Featured Perspectives On Current Science, Perspectives on Current Science|

Footnote from title: modified slightly from “A brief history of oligonucleotide therapeutics” in the Timmerman Report, copyright 2022, and reprinted with permission. A Brief History of Oligonucleotide Therapeutics About 50 years ago, several scientists independently conceived of the idea of blocking gene expression with ...

Eplontersen May Soon Provide Another Safe, Effective Treatment for People Diagnosed with ATTR

September 23rd, 2022|Categories: Featured Perspectives On Current Science, Perspectives on Current Science|

People who have been diagnosed with hereditary transthyretin amyloidosis (ATTRv) may soon have the option of choosing another safe, effective therapy, one that significantly improves quality of life, according to patients who received it in the clinical trial. ATTRv is a progressive, debilitating, ...

A Landmark Permanent Treatment for Children Born with a Deadly Immune Disorder

August 27th, 2022|Categories: Featured Perspectives On Current Science, Perspectives on Current Science|

In June 2022, the first stem cell gene therapy of Dutch origin was successfully given to a patient by researchers at the Leiden University Medical Centre (LUMC). A baby with severe congenital immune disorder (SCID) received the complex but one-time treatment, marking the first ...

Could Artificial Intelligence Provide the Key to Life Saving Medicines?

May 9th, 2022|Categories: Featured Perspectives On Current Science, Perspectives on Current Science|

Drug discovery is time consuming and expensive, requiring trial and error screening. This means that many people have to wait decades, or a lifetime, to find a treatment for their disease. Others, especially those with rare diseases, may never have hope of a treatment. ...

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