Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent Porphyria
Sardh E, Harper P, Balwani M, Stein P, Rees D, Bissell DM, Desnick R, Parker C, Phillips J, Bonkovsky HL, Vassiliou D, Penz C, Chan-Daniels A, He Q, Querbes W, Fitzgerald K, Kim JB, Garg P, Vaishnaw A, Simon AR, Anderson KE. N Engl J ...
2019 Dr. Alan M. Gewirtz Memorial Scholarship Winner: Bruno M.D.C. Godinho, PhD
Bruno M.D.C. Godinho, PhD RNA Therapeutics Institute, UMass Medical School Biography: Bruno Godinho received his PhD in Pharmacy from University College Cork (Ireland) in 2014, where he studied formulation-based approaches for siRNA delivery to the central nervous system (CNS). His work from graduate school ...
Interview with Daniel O’Reilly, PhD Candidate
Daniel O’Reilly MChem, PhD Candidate McGill University  How did you become interested in the field of oligonucleotides? My introduction to the world of genetic disease and oligonucleotides came at an early age when my mum was diagnosed with Huntington’s Disease (HD). Witnessing the ...