Treatment of a metabolic liver disease by in vivo genome base editing in adult mice

Villiger L, Grisch-Chan HM, Lindsay H, Ringnalda F, Pogliano CB, Allegri G, Fingerhut R, Häberle J, Matos J, Robinson MD, Thöny B, Schwank G.
Nat Med. 2018 Oct;24(10):1519-1525.

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