In vivo base editing restores sensory transduction and transiently improves auditory function in a mouse model of recessive deafness

Yeh WH, Shubina-Oleinik O, Levy JM, Pan B, Newby GA, Wornow M, Burt R, Chen JC, Holt JR, Liu DR.

Sci Transl Med. 2020 Jun 3;12(546):eaay9101.

Pubmed