2017 Oligonucleotide Therapeutics Education Workshop
Designing Oligo Therapeutics and Understanding Their PK
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Target Knock Down – ASOs and siRNA
Chris Hart, PhD, Ionis Pharmaceuticals and Martin Maier, PhD, Alnylam Pharma
CRISPR Approaches
Rachel Haurwitz, PhD, Caribou Biosciences
mRNA
Matthew Stanton, PhD, Moderna Therapeutics
Immune Stimulatory Oligos
Art Krieg, MD, Checkmate Pharmaceuticals
PK and Biodistribution
Richard Geary, PhD, Ionis Pharmaceuticals
AON Safety Screening – In vitro Assays Capturing Toxicity Risks
Sabine Sewing, PhD, Hoffmann-La Roche, Roche Innovation Center
RNAi Drug Discovery
Martin Maier, PhD, Alnylam Pharma
Q&A
Speaker Panel
2017 Annual Meeting – Welcome
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Welcome & Opening Remarks
OTS President: Arthur M. Krieg, MD, Checkmate Pharmaceuticals
2017 Annual Meeting Keynote
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Keynote Presentation
A Worms Tale: Oligonucleotide-Guided Gene Regulation and Secrets of Inheritance and Immortality
Craig C. Mello, PhD, RNA Therapeutics Institute, University of Massachusetts Medical School
2017 Annual Meeting Award Winner Presentations
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Young Investigator Award
Keith Gagnon, PhD, Southern Illinois University
Paper of the Year Award
Richard Finkel, MD, Nemours Children’s Hospital
Gewirtz Memorial Scholarship Award
Karyn Schmidt, PhD, Dana-Farber Cancer Institute
2017 Annual Meeting Lifetime Achievement
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Lifetime Achievement Award
Michael J. Gait, PhD, Medical Research Council, Laboratory of Molecular Biology