Exon Junction Complexes Suppress Spurious Splice Sites to Safeguard Transcriptome Integrity
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Modulation of MKNK2 alternative splicing by splice-switching oligonucleotides as a novel approach for glioblastoma treatment
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Genetic Modulation of RNA Splicing with a CRISPR-Guided Cytidine Deaminase
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Evaluation of the effect of 2′-O-methyl, fluoro hexitol, bicyclo and Morpholino nucleic acid modifications on potency of GalNAc conjugated antisense oligonucleotides in mice
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Single-Stranded Nucleic Acids Regulate TLR3/4/7 Activation through Interference with Clathrin-Mediated Endocytosis
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CRISPR-induced exon skipping is dependent on premature termination codon mutations
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Therapeutic Oligonucleotides: State of the Art
Smith CIE, Zain R. Annu Rev Pharmacol Toxicol. 2018 Oct 4. PubMed
Cell-Penetrating Peptide Conjugates of Steric Blocking Oligonucleotides as Therapeutics for Neuromuscular Diseases from a Historical Perspective to Current Prospects of Treatment
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Splice-Modulating Oligonucleotide QR-110 Restores CEP290 mRNA and Function in Human c.2991+1655A>G LCA10 Models
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Morpholino Antisense Oligomers as a Potential Therapeutic Option for the Correction of Alternative Splicing in PMD, SPG2, and HEMS
Tantzer S, Sperle K, Kenaley K, Taube J, Hobson GM. Mol Ther Nucleic Acids. 2018 Sep 7;12:420-432. PubMed