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Technical Considerations for Use of Oligonucleotide Solution API
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Safety, Tolerability, and Efficacy of Viltolarsen in Boys with Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial
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Glycine Enhances Satellite Cell Proliferation, Cell Transplantation, and Oligonucleotide Efficacy in Dystrophic Muscle
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Delivery of oligonucleotides to bone marrow to modulate ferrochelatase splicing in a mouse model of erythropoietic protoporphyria
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Fetal antisense oligonucleotide therapy for congenital deafness and vestibular dysfunction
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Detailed cellular assessment of albumin-bound oligonucleotides: Increased stability and lower non-specific cell uptake
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