Delivery of GalNAc-Conjugated Splice-Switching ASOs to Non-hepatic Cells through Ectopic Expression of Asialoglycoprotein Receptor
Delivery of GalNAc-Conjugated Splice-Switching ASOs to Non-hepatic Cells through Ectopic Expression of Asialoglycoprotein Receptor …………… Scharner J, Qi S, Rigo F, Bennett CF, Krainer AR. Mol Ther Nucleic Acids. 2019 Jun 7;16:313-325. PubMed 00