Antisense Oligonucleotide Mediated Splice Correction of a Deep Intronic Mutation in OPA1
Antisense Oligonucleotide Mediated Splice Correction of a Deep Intronic Mutation in OPA1 …………… Bonifert T, Gonzalez Menendez I, Battke F, Theurer Y, Synofzik M, Schöls L, Wissinger B. Mol Ther Nucleic Acids. 2016 Nov 22;5(11):e390. PubMed 00