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Oligonucleotide therapy mitigates disease in Spinocerebellar Ataxia Type 3 mice …………… McLoughlin HS, Moore LR, Chopra R, Komlo R, McKenzie M, Blumenstein KG, Zhao H, Kordasiewicz HB, Shakkottai VG, Paulson HL. Ann Neurol. 2018 Jun 16. PubMed 00
CHP1 reduction ameliorates spinal muscular atrophy pathology by restoring calcineurin activity and endocytosis …………… Janzen E, Mendoza-Ferreira N, Hosseinibarkooie S, Schneider S, Hupperich K, Tschanz T, Grysko V, Riessland M, Hammerschmidt M, Rigo F, Bennett CF, Kye MJ, Torres-Benito L, Wirth B. Brain. 2018 Jun 28. PubMed 00
Gene Therapy for Neuropathic Pain through siRNA-IRF5 Gene Delivery with Homing Peptides to Microglia …………… Terashima T, Ogawa N, Nakae Y, Sato T, Katagi M, Okano J, Maegawa H, Kojima H. Mol Ther Nucleic Acids. 2018 Jun 1;11:203-215. PubMed 00