Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis …………… Adams D, Gonzalez-Duarte A, O’Riordan WD, Yang CC, Ueda M, Kristen AV, Tournev I, Schmidt HH, Coelho T, Berk JL, Lin KP, Vita G, Attarian S, Planté-Bordeneuve V, Mezei MM, Campistol JM, Buades J, Brannagan TH 3rd, Kim BJ, Oh J, Parman Y, Sekijima Y, Hawkins…