Exon-Skipping Oligonucleotides Restore Functional Collagen VI by Correcting a Common COL6A1 Mutation in Ullrich CMD
Aguti S, Bolduc V, Ala P, Turmaine M, Bönnemann CG, Muntoni F, Zhou H. Mol Ther Nucleic Acids. 2020 Jun 1;21:205-216. Pubmed
Argonaute binding within 3′-untranslated regions poorly predicts gene repression
Chu Y, Kilikevicius A, Liu J, Johnson KC, Yokota S, Corey DR. Nucleic Acids Res. 2020 Jun 5:gkaa478. Pubmed
MicroRNA-206 Regulates Stress-Provoked Aggressive Behaviors in Post-weaning Social Isolation Mice
Chang CH, Kuek EJW, Su CL, Gean PW. Mol Ther Nucleic Acids. 2020 Jun 5;20:812-822. Pubmed
A systems approach delivers a functional microRNA catalog and expanded targets for seizure suppression in temporal lobe epilepsy
Venø MT, Reschke CR, Morris G, Connolly NMC, Su J, Yan Y, Engel T, Jimenez-Mateos EM, Harder LM, Pultz D, Haunsberger SJ, Pal A, Heller JP, Campbell A, Langa E, Brennan GP, Conboy K, Richardson A, Norwood BA, Costard LS, Neubert V, Del Gallo F, ...
Reversing a model of Parkinson’s disease with in situ converted nigral neurons
Qian H, Kang X, Hu J, Zhang D, Liang Z, Meng F, Zhang X, Xue Y, Maimon R, Dowdy SF, Devaraj NK, Zhou Z, Mobley WC, Cleveland DW, Fu XD. Nature. 2020 Jun;582(7813):550-556. Pubmed