Treatment of Hemophilia A Using Factor VIII Messenger RNA Lipid Nanoparticles
Chen CY, Tran DM, Cavedon A, Cai X, Rajendran R, Lyle MJ, Martini PGV, Miao CH. Mol Ther Nucleic Acids. 2020 Apr 7;20:534-544 PubMed
Engineered Circular RNA Sponges Act as miRNA Inhibitors to Attenuate Pressure Overload-Induced Cardiac Hypertrophy
Lavenniah A, Luu TDA, Li YP, Lim TB, Jiang J, Ackers-Johnson M, Foo RS. Mol Ther. 2020 Apr 14. pii: S1525-0016(20)30187-8. PubMed
Genomic Clustering Facilitates Nuclear Processing of Suboptimal Pri-miRNA Loci
Shang R, Baek SC, Kim K, Kim B, Kim VN, Lai EC. Mol Cell. 2020 Apr 16;78(2):303-316.e4. PubMed
MicroRNA Clustering Assists Processing of Suboptimal MicroRNA Hairpins through the Action of the ERH Protein
Fang W, Bartel DP. Mol Cell. 2020 Apr 16;78(2):289-302.e6. PubMed
CRISPR-Based Therapeutic Genome Editing: Strategies and In Vivo Delivery by AAV Vectors
Wang D, Zhang F, Gao G. Cell. 2020 Apr 2;181(1):136-150. PubMed