Targeted Delivery of C/EBPα-saRNA by RNA Aptamers Shows Anti-tumor Effects in a Mouse Model of Advanced PDAC
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Discovery and preclinical evaluation of anti-miR-17 oligonucleotide RGLS4326 for the treatment of polycystic kidney disease
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Combining Engineered U1 snRNA and Antisense Oligonucleotides to Improve the Treatment of a BBS1 Splice Site Mutation
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Suppression of Mutant Protein Expression in SCA3 and SCA1 Mice Using a CAG Repeat-Targeting Antisense Oligonucleotide
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CRISPR-Cas9-based mutagenesis frequently provokes on-target mRNA misregulation
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CRISPR DNA base editors with reduced RNA off-target and self-editing activities
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Click-Particle Display for Base-Modified Aptamer Discovery
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Massively parallel RNA device engineering in mammalian cells with RNA-Seq
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An in Vivo miRNA Delivery System for Restoring Infarcted Myocardium
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