Pnpla3 silencing with antisense oligonucleotides ameliorates nonalcoholic steatohepatitis and fibrosis in Pnpla3 I148M knock-in mice
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CCR5 Is a Therapeutic Target for Recovery after Stroke and Traumatic Brain Injury
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IONIS-PKKRx a Novel Antisense Inhibitor of Prekallikrein and Bradykinin Production
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Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent Porphyria
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Antisense Inhibition of Glucagon Receptor by IONIS-GCGRRx Improves Type 2 Diabetes Without Increase in Hepatic Glycogen Content in Patients With Type 2 Diabetes on Stable Metformin Therapy
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Optimization of Lipid Nanoparticles for Intramuscular Administration of mRNA Vaccines
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