Extrahepatic Targeting of Oligonucleotides with Receptor-Binding Non-immunoglobulin Scaffold Proteins
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Improving Small Interfering RNA Delivery In Vivo Through Lipid Conjugation
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Clinical utility of circulating non-coding RNAs – an update
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Artificially Expanded Genetic Information Systems for New Aptamer Technologies
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Riboswitches and Translation Control
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Eradication of spontaneous malignancy by local immunotherapy
Sagiv-Barfi I, Czerwinski DK, Levy S, Alam IS, Mayer AT, Gambhir SS, Levy R. Idit Sagiv Barfi and Ronald Levy Sci Transl Med. 2018 Jan 31;10(426). Inducing a cancer patient’s own immune system to recognize and attack tumours is the goal of immunotherapy ...
Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia
An D, Schneller JL, Frassetto A, Liang S, Zhu X, Park JS, Theisen M, Hong SJ, Zhou J, Rajendran R, Levy B, Howell R, Besin G, Presnyak V, Sabnis S, Murphy-Benenato KE, Kumarasinghe ES, Salerno T, Mihai C, Lukacs CM, Chandler RJ, Guey LT, Venditti ...
Interview with Annika de Jong, MSc, PhD Candidate
The first internship of my master was performed at the department of Human Genetics at the Leiden University Medical Centre where Prof. AnnemiekeAartsma-Rus
Single Intramuscular Injection of AAV-shRNA Reduces DNM2 and Prevents Myotubular Myopathy in Mice
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Systemic delivery of BACE1 siRNA through neuron-targeted nanocomplexes for treatment of Alzheimer’s disease
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