Antisense oligonucleotides correct the familial dysautonomia splicing defect in IKBKAP transgenic mice

September 27th, 2018|Categories: Paper of the Month|

Sinha R, Kim YJ, Nomakuchi T, Sahashi K, Hua Y, Rigo F, Bennett CF, Krainer AR. Nucleic Acids Res. 2018 Jun 1;46(10):4833-4844. The three joint first authors: Rahul Sinha Young Jin Kim Tomoki Nomakuchi Currently, the most successful oligonucleotide ...

Go to Top